Gene editing has delivered remarkable results against sickle cell disease. Now researchers are working to make these personalized treatments faster, cheaper, and available to far more patients.

The first person to ever be cured of sickle cell anemia in Louisiana received revolutionary gene therapy. The treatment is now offered at this hospital.

Within 12 hours of landing in Florida in January, 2021, Sebastien Beauzile, then 17, was admitted to two separate hospitals. He had come to Florida to surprise his sister for her birthday. But instead ...

HBB-β S: An A greater than T point mutation results in the substitution of glutamate for valine in the sixth amino acid position (or seventh, if the… Development of SCD depends on whether the ...

Right now, approximately 20 billion red blood cells are busy traveling through your blood vessels. They are delivering oxygen to all the different tissues in your body and removing carbon dioxide to ...

He's the first in New York to receive the novel treatment and one of the first in the world. Share on Facebook (opens in a new window) Share on X (opens in a new window) Share on Reddit (opens in a ...

Though he doesn't remember it, Branden Baptiste had his first sickle cell crisis at age 2. Through elementary school, he was in and out of the hospital with pain episodes, not knowing why. As he got ...

WASHINGTON - The Food and Drug Administration Wednesday granted supplemental approval for a breakthrough CRISPR gene therapy medication, making it the first available to treat young children with ...

Lauren Pastrana is the co-anchor of CBS4 News weeknights at 5, 6, 7 and 11 p.m. She joined CBS Miami in April 2012 as a reporter. She is an Emmy-nominated, multimedia journalist with experience in ...

Daniel Cressy's illness was a barrier to getting his pilot's license, until a novel treatment was approved in the United ...