Muscular Dystrophy News13h
MD trial update: 5 OPMD patients safely treated with gene therapy
Five oculopharyngeal muscular dystrophy (OPMD) patients have now been treated with the gene therapy candidate BB-301 in a ...
Muscular Dystrophy News5d
Phase 1 trial of SAT-3247 finishes enrolling healthy volunteers
Enrollment of healthy volunteers for a Phase 1 trial testing Duchenne muscular dystrophy (DMD) treatment candidate SAT-3247 ...
Muscular Dystrophy News6d
It started with shoes, but now everything is too heavy
FSHD has made an increasing number of everyday items unusable for columnist Robin Stemple because they're too heavy.
Muscular Dystrophy News4d
A week in the life of an overwhelmed caregiver
Providing care for three boys with DMD while holding down a job isn't easy for columnist Betty Vertin, who is an overwhelmed caregiver.